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Chembiomed, Ltd. — Rare Disease Pipeline | Kisho | Kisho
Chembiomed, Ltd.
Other
4
Orphan Designations
0
FDA Approvals
12
Rare Diseases
0
News Articles
Pipeline
Designations
News
Diseases
Disease
Drug(s)
Designation
Approved
DYRK1A-related intellectual disability syndrome
Trisaccharides A and B
Orphan Designation
-
alopecia-intellectual disability syndrome 2
Trisaccharides A and B
Orphan Designation
-
anosmia for isobutyric acid
Trisaccharides A and B
Orphan Designation
-
blood coagulation disease
Trisaccharides A and B
Orphan Designation
-
blood platelet disease
Trisaccharides A and B
Orphan Designation
-
congenital microcephaly - severe encephalopathy - progressive cerebral atrophy syndrome
Trisaccharides A and B
Orphan Designation
-
malignant type AB thymoma
Trisaccharides A and B
Orphan Designation
-
neonatal encephalomyopathy-cardiomyopathy-respiratory distress syndrome
Trisaccharides A and B
Orphan Designation
-
neuroacanthocytosis
Trisaccharides A and B
Orphan Designation
-
severe intellectual disability-short stature-behavioral abnormalities-facial dysmorphism syndrome
Trisaccharides A and B
Orphan Designation
-
thymoma type AB
Trisaccharides A and B
Orphan Designation
-
xerosis and growth failure with immune and pulmonary dysfunction syndrome
Trisaccharides A and B
Orphan Designation
-
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