2
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| adult acute respiratory distress syndrome | perfluorooctyl-bromide (PFOB) | Orphan Designation | - |
| congenital multicore myopathy with external ophthalmoplegia | perfluorooctyl-bromide | Orphan Designation | - |
| congenital total pulmonary venous return anomaly | perfluorooctyl-bromide | Orphan Designation | - |
| newborn respiratory distress syndrome | perfluorooctyl-bromide (PFOB) | Orphan Designation | - |
| respiratory distress syndrome in premature infants | perfluorooctyl-bromide (PFOB) | Orphan Designation | - |
| tetrasomy 12p | perfluorooctyl-bromide | Orphan Designation | - |