5
Orphan Designations
0
FDA Approvals
15
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Angelman syndrome | Alpha-1-antitrypsin (recombinant DNA Origin) | Orphan Designation | - |
| acute myeloid leukemia | Aldesleukin | Orphan Designation | - |
| aortic valve disease 1 | Alpha-1-antitrypsin (recombinant DNA Origin) | Orphan Designation | - |
| aortic valve stenosis | Alpha-1-antitrypsin (recombinant DNA Origin) | Orphan Designation | - |
| cataract 13 with adult I phenotype | Proleukin | Orphan Designation | - |
| clear cell renal carcinoma | Proleukin | Orphan Designation | - |
| inborn error of immunity | PEG-interleukin-2 | Orphan Designation | - |
| latent autoimmune diabetes in adults | Proleukin | Orphan Designation | - |
| metastatic malignant neoplasm in the colon | Proleukin | Orphan Designation | - |
| metastatic malignant neoplasm in the lymph nodes | Proleukin | Orphan Designation | - |
| metastatic melanoma | Proleukin | Orphan Designation | - |
| metastatic neoplasm | Proleukin | Orphan Designation | - |
| nut midline carcinoma | Proleukin | Orphan Designation | - |
| primary biliary cholangitis | PEG-interleukin-2 | Orphan Designation | - |
| primary cutaneous lymphoma | PEG-interleukin-2 | Orphan Designation | - |