1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| developmental and epileptic encephalopathy, 24 | 2-butyl-9-methyl-8-(2H-1,2,3-triazol-2-yl)-9H-purin-6-amine A triazole purine analogue | Orphan Designation | - |
| intellectual disability, autosomal dominant 24 | 2-butyl-9-methyl-8-(2H-1,2,3-triazol-2-yl)-9H-purin-6-amine A triazole purine analogue | Orphan Designation | - |
| non-24-hour sleep-wake syndrome | 2-butyl-9-methyl-8-(2H-1,2,3-triazol-2-yl)-9H-purin-6-amine A triazole purine analogue | Orphan Designation | - |