5
Orphan Designations
1
FDA Approvals
12
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| ALG3-congenital disorder of glycosylation | Amifostine | Orphan Designation | - |
| Leber congenital amaurosis | Amifostine | Orphan Designation | - |
| Luscan-Lumish syndrome | Amifostine | Orphan Designation | - |
| Wolf-Hirschhorn syndrome | Amifostine | Orphan Designation | - |
| advanced sleep phase syndrome | Amifostine | Orphan Designation | - |
| autoimmune disorder of the nervous system | Amifostine | Orphan Designation | - |
| autosomal semi-dominant severe lipodystrophic laminopathy | Amifostine | Orphan Designation | - |
| dermatitis, atopic, 8 | Amifostine | Orphan Designation | - |
| metastatic melanoma | Amifostine | Orphan Designation | - |
| myelodysplastic syndrome | Amifostine | Orphan Designation | - |
| retinitis | FOSCAVIR | - | FDA Approved |
| streptococcus, group A, severity of infection by | Amifostine | Orphan Designation | - |