1
Orphan Designations
4
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| DYRK1A-related intellectual disability syndrome | spironolactone | Orphan Designation | - |
| Huntington disease | spironolactone | Orphan Designation | - |
| myoclonic dystonia 11 | spironolactone | Orphan Designation | - |