4
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| glioma susceptibility 4 | abeotaxane inhibitor of microtubules | Orphan Designation | - |
| malignant glioma | Berubicin | Orphan Designation | - |
| mixed glioma | abeotaxane inhibitor of microtubules | Orphan Designation | - |
| optic pathway glioma | abeotaxane inhibitor of microtubules | Orphan Designation | - |
| pediatric hepatocellular carcinoma | abeotaxane inhibitor of microtubules | Orphan Designation | - |
| pediatric ovarian dysgerminoma | abeotaxane inhibitor of microtubules | Orphan Designation | - |
| pediatric-onset Graves disease | abeotaxane inhibitor of microtubules | Orphan Designation | - |
| progressive supranuclear palsy | (2'R,3'S)-2'-hydroxy-N-carboxy-3'-amino-5'-methyl-hexanoic,N-tert-butyl ester, 13 ester 5B-20-epoxy-1B,2a,4a,7B,9a,10a,13a-heptahydroxy-4,10-diacetate-2-benzoate-(1"S)-7,9-acrolein acetal-11(15-1)-abeotaxane | Orphan Designation | - |