2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| malignant carotid body paraganglioma | Small molecule activator of pantothenate kinases | Orphan Designation | - |
| post-treatment Lyme disease syndrome | Small molecule activator of pantothenate kinases | Orphan Designation | - |
| propionic acidemia | Small molecule activator of pantothenate kinases | Orphan Designation | - |
| treatment-refractory schizophrenia | Small molecule activator of pantothenate kinases | Orphan Designation | - |