1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Lafora disease | metformin | Orphan Designation | - |
| progressive myoclonic epilepsy type 6 | metformin | Orphan Designation | - |
| progressive myoclonic epilepsy type 7 | metformin | Orphan Designation | - |