4
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Duchenne muscular dystrophy | angiotensin (1-7)[A(1-7)] | Orphan Designation | - |
| LAMA2-related muscular dystrophy | Angiotensin (1-7) | Orphan Designation | - |
| centripetalis recessive dystrophic epidermolysis bullosa | Angiotensin (1-7) | Orphan Designation | - |
| limb-girdle muscular dystrophy | Angiotensin (1-7) | Orphan Designation | - |
| recessive dystrophic epidermolysis bullosa | Angiotensin (1-7) | Orphan Designation | - |
| recessive dystrophic epidermolysis bullosa inversa | Angiotensin (1-7) | Orphan Designation | - |