1
Orphan Designations
0
FDA Approvals
1
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Crouzon syndrome-acanthosis nigricans syndrome | autologous ex vivo expanded polyclonal CD4plusCD25plusCD127 lo/- FOXP3plus regulatory T cells (CELZ-101) | Orphan Designation | - |