4
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| T-cell non-Hodgkin lymphoma | Allogeneic CRISPR/Cas9-mediated genetically modified CAR T cells targeting CD70 antigen | Orphan Designation | - |
| acute lymphoblastic leukemia | allogeneic CRISPR/Cas9-mediated genetically modified CAR T cells targeting CD19 antigen | Orphan Designation | - |
| follicular lymphoma | allogeneic CRISPR/Cas9-mediated genetically modified CAR T cells targeting CD19 antigen | Orphan Designation | - |
| plasma cell myeloma | allogeneic CRISPR/Cas9-mediated genetically modified CAR T cells targeting B-cell maturation antigen | Orphan Designation | - |