1
Orphan Designations
3
FDA Approvals
5
Rare Diseases
1
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Gorham-Stout disease | Harliku | Orphan Designation | - |
| alkaptonuria | Harliku | Orphan Designation | - |
| fibrous dysplasia | Harliku | Orphan Designation | - |
| medial condensing osteitis of the clavicle | Harliku | Orphan Designation | - |
| osteogenesis imperfecta and a reduction of bone mineral density. | Harliku | Orphan Designation | - |