1
Orphan Designations
0
FDA Approvals
2
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| arteriovenous malformations of the brain | alteplase | Orphan Designation | - |
| chromosome 4Q32.1-q32.2 triplication syndrome | alteplase | Orphan Designation | - |