1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Luscan-Lumish syndrome | Triptorelin pamoate | Orphan Designation | - |
| advanced sleep phase syndrome | Triptorelin pamoate | Orphan Designation | - |
| autosomal semi-dominant severe lipodystrophic laminopathy | Triptorelin pamoate | Orphan Designation | - |