2
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Bicervical bicornuate uterus with patent cervix and vagina | ferric hexacyanoferrate (II) "Prussian Blue" | Orphan Designation | - |
| DYRK1A-related intellectual disability syndrome | Mesnex | Orphan Designation | - |
| anosmia for isobutyric acid | Mesnex | Orphan Designation | - |
| carbon monoxide-induced delayed encephalopathy | ferric hexacyanoferrate (II) "Prussian Blue" | Orphan Designation | - |
| natal teeth-intestinal pseudoobstruction-patent ductus syndrome | ferric hexacyanoferrate (II) "Prussian Blue" | Orphan Designation | - |
| neuroacanthocytosis | Mesnex | Orphan Designation | - |