2
Orphan Designations
1
FDA Approvals
9
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| 7q11.23 microduplication syndrome | Intraoral fluoride releasing system | Orphan Designation | - |
| Dowling-Degos disease 4 | Buffered Ursodeoxycholic Acid | Orphan Designation | - |
| Potocki-Lupski syndrome | Intraoral fluoride releasing system | Orphan Designation | - |
| Rubinstein-Taybi syndrome due to EP300 haploinsufficiency | Intraoral fluoride releasing system | Orphan Designation | - |
| chromosome 16p13.3 duplication syndrome | Intraoral fluoride releasing system | Orphan Designation | - |
| congenital myopathy 2a, typical, autosomal dominant | Intraoral fluoride releasing system | Orphan Designation | - |
| hereditary sensory and autonomic neuropathy type 7 | Buffered Ursodeoxycholic Acid | Orphan Designation | - |
| hypotrichosis 6 | Buffered Ursodeoxycholic Acid | Orphan Designation | - |
| malignant tumor of neck | Intraoral fluoride releasing system | Orphan Designation | - |