5
Orphan Designations
0
FDA Approvals
9
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Eisenmenger syndrome | cardiotrophin-1 | Orphan Designation | - |
| acute liver failure | cardiotrophin-1 | Orphan Designation | - |
| brain ischemia | cardiotrophin-1 | Orphan Designation | - |
| ischemia reperfusion injury | cardiotrophin-1 | Orphan Designation | - |
| liver disease, severe congenital | cardiotrophin-1 | Orphan Designation | - |
| localized scleroderma | Peptide 144 TGF beta-1-inhibitor | Orphan Designation | - |
| pseudo-TORCH syndrome 1 | cardiotrophin-1 | Orphan Designation | - |
| retinal ischemia | cardiotrophin-1 | Orphan Designation | - |
| systemic sclerosis | peptide 144 TGF beta-1 inhibitor | Orphan Designation | - |