3
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| cerebrotendinous xanthomatosis | Chenodeoxycholic acid | Orphan Designation | - |
| eosinophilic esophagitis | budesonide | Orphan Designation | - |
| primary sclerosing cholangitis | Norucholic acid | Orphan Designation | - |