1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| primary systemic amyloidosis | sodium dichloroacetate | Orphan Designation | - |
| systemic lupus erythematosus | sodium dichloroacetate | Orphan Designation | - |
| systemic sclerosis | sodium dichloroacetate | Orphan Designation | - |