3
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Char syndrome | Sodium phenylbutyratePhenylacetate | Orphan Designation | - |
| acute promyelocytic leukemia | Phenylbutyrate | Orphan Designation | - |
| aldosterone-producing adenoma with seizures and neurological abnormalities | Sodium phenylbutyratePhenylacetate | Orphan Designation | - |
| ciliary dyskinesia, primary, 40 | Sodium phenylbutyratePhenylacetate | Orphan Designation | - |