3
Orphan Designations
0
FDA Approvals
9
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| GM1 gangliosidosis | Human Insulin (rDNA) | Orphan Designation | - |
| chylomicron retention disease | recombinant human insulin | Orphan Designation | - |
| congenital short bowel syndrome | human insulin (rDNA) | Orphan Designation | - |
| exudative vitreoretinopathy 1 | Human Insulin (rDNA) | Orphan Designation | - |
| intestinal hypomagnesemia 1 | recombinant human insulin | Orphan Designation | - |
| mitochondrial DNA depletion syndrome 4b | recombinant human insulin | Orphan Designation | - |
| retinopathy of prematurity | Human Insulin (rDNA) | Orphan Designation | - |
| secondary short bowel syndrome | human insulin (rDNA) | Orphan Designation | - |
| short bowel syndrome | human insulin (rDNA) | Orphan Designation | - |