2
Orphan Designations
0
FDA Approvals
9
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| MAX-related tumor predisposition | Infumorph | Orphan Designation | - |
| May-Thurner syndrome | Infumorph | Orphan Designation | - |
| chronic hiccup | Infumorph | Orphan Designation | - |
| esophageal varices | Sodium tetradecyl sulfate | Orphan Designation | - |
| headache disorder | Infumorph | Orphan Designation | - |
| intractable diarrhea-choanal atresia-eye anomalies syndrome | Infumorph | Orphan Designation | - |
| mal de Debarquement | Infumorph | Orphan Designation | - |
| mal de Meleda | Infumorph | Orphan Designation | - |
| myoclonus, intractable, neonatal | Infumorph | Orphan Designation | - |