2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Wolf-Hirschhorn syndrome | etarfolatide | Orphan Designation | - |
| double nail for fifth toe | etarfolatide | Orphan Designation | - |
| ovarian cancer | vintafolide | Orphan Designation | - |
| spatial visualization, aptitude for | etarfolatide | Orphan Designation | - |