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Eton Pharmaceuticals, Inc. — Rare Disease Pipeline | Kisho | Kisho
Eton Pharmaceuticals, Inc.
Other
3
Orphan Designations
4
FDA Approvals
19
Rare Diseases
0
News Articles
Pipeline
Designations
News
Diseases
Disease
Drug(s)
Designation
Approved
Bethlem myopathy 1A
Khindivi
Orphan Designation
-
COG4-congenital disorder of glycosylation
Increlex
Orphan Designation
-
Mowat-Wilson syndrome
Galzin
Orphan Designation
-
Wilson disease
Galzin
Orphan Designation
-
adrenocortical carcinoma, hereditary
Khindivi
Orphan Designation
-
alternating hemiplegia of childhood
Khindivi
Orphan Designation
-
carbon monoxide-induced delayed encephalopathy
Galzin
Orphan Designation
-
cardiomyopathy, familial hypertrophic, 31
Khindivi
Orphan Designation
-
cerebrooculofacioskeletal syndrome 4
Increlex
Orphan Designation
-
congenital myopathy 26
Khindivi
Orphan Designation
-
glycogen storage disease VI
Increlex
Orphan Designation
-
growth hormone insensitivity syndrome
Increlex
Orphan Designation
-
inflammatory bowel disease 1
Increlex
Orphan Designation
-
multisystemic smooth muscle dysfunction syndrome
Galzin
Orphan Designation
-
natal teeth-intestinal pseudoobstruction-patent ductus syndrome
Galzin
Orphan Designation
-
pediatric hepatocellular carcinoma
Khindivi
Orphan Designation
-
pediatric ovarian dysgerminoma
Khindivi
Orphan Designation
-
pediatric-onset Graves disease
Khindivi
Orphan Designation
-
severe growth deficiency-strabismus-extensive dermal melanocytosis-intellectual disability syndrome
Increlex
Orphan Designation
-
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