1
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Niemann-Pick disease, type C2 | Lumryz | Orphan Designation | - |
| narcolepsy | Lumryz | Orphan Designation | - |
| narcolepsy 1 | Lumryz | Orphan Designation | - |
| narcolepsy without cataplexy | Lumryz | Orphan Designation | - |
| narcolepsy-cataplexy syndrome | Lumryz | Orphan Designation | - |