2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Kaposi's sarcoma | alitretinoin | Orphan Designation | - |
| cystic fibrosis | N-acetylcysteinate Lysine | Orphan Designation | - |
| developmental and epileptic encephalopathy 119 | alitretinoin | Orphan Designation | - |
| oculodentodigital dysplasia | alitretinoin | Orphan Designation | - |