1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Alstrom syndrome | Intravenous immune globulin | Orphan Designation | - |
| Finnish type amyloidosis | Intravenous immune globulin | Orphan Designation | - |
| lysinuric protein intolerance | Intravenous immune globulin | Orphan Designation | - |