3
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Huntington disease | ubiquinol | Orphan Designation | - |
| mitochondrial myopathy with diabetes | Ubiquinone | Orphan Designation | - |
| pediatric hepatocellular carcinoma | Ubiquinol, coenzyme Q10, ubiquinone | Orphan Designation | - |
| pediatric ovarian dysgerminoma | Ubiquinol, coenzyme Q10, ubiquinone | Orphan Designation | - |
| pediatric-onset Graves disease | Ubiquinol, coenzyme Q10, ubiquinone | Orphan Designation | - |
| spastic paraplegia, mitochondrial | Ubiquinone | Orphan Designation | - |
| striatonigral degeneration, infantile, mitochondrial | Ubiquinone | Orphan Designation | - |