1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| chronic graft versus host disease | aganirsen | Orphan Designation | - |
| corneal disorder | aganirsen | Orphan Designation | - |
| corneal dystrophy | aganirsen | Orphan Designation | - |