2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| renal cell carcinoma | Recombinant human interleukin-12 | Orphan Designation | - |
| severe Canavan disease | Neumega | Orphan Designation | - |
| severe achondroplasia-developmental delay-acanthosis nigricans syndrome | Neumega | Orphan Designation | - |
| severe neonatal-onset encephalopathy with microcephaly | Neumega | Orphan Designation | - |