1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Spondyloenchondrodysplasia with immune dysregulation | Wayrilz | Orphan Designation | - |
| acquired purpura fulminans | Wayrilz | Orphan Designation | - |
| adult pleomorphic rhabdomyosarcoma | Wayrilz | Orphan Designation | - |
| adult-onset non-insulinoma persistent hyperinsulinemic hypoglycemia | Wayrilz | Orphan Designation | - |
| autoimmune thrombocytopenic purpura | Wayrilz | Orphan Designation | - |
| primary adult heart tumor | Wayrilz | Orphan Designation | - |