1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| anatomical narrow angle borderline glaucoma | adenoviral vector expressing the E.coli purine nucleoside phosphorylase gene and fludarabine | Orphan Designation | - |
| chronic closed-angle glaucoma | adenoviral vector expressing the E.coli purine nucleoside phosphorylase gene and fludarabine | Orphan Designation | - |
| inflammatory disease | adenoviral vector expressing the E.coli purine nucleoside phosphorylase gene and fludarabine | Orphan Designation | - |