1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Nezelof syndrome | hyaluronic acid | Orphan Designation | - |
| alpha 1-antitrypsin deficiency | hyaluronic acid | Orphan Designation | - |
| interstitial lung disease due to ABCA3 deficiency | hyaluronic acid | Orphan Designation | - |