3
Orphan Designations
0
FDA Approvals
5
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute chest syndrome | Oxbryta | Orphan Designation | - |
| hereditary persistence of fetal hemoglobin-sickle cell disease syndrome | Oxbryta | Orphan Designation | - |
| sickle cell disease | Inclacumab(S)-2-hydroxy-6-((4-(2-(2-hydroxyethyl)nicotinoyl)morpholin- 3-yl)methoxy)benzaldehydeOxbryta | Orphan Designation | - |
| sickle cell-hemoglobin c disease syndrome | Oxbryta | Orphan Designation | - |
| sickle cell-hemoglobin d disease syndrome | Oxbryta | Orphan Designation | - |