2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute lymphoblastic leukemia | Talotrexin | Orphan Designation | - |
| brain glioma | 5-iodo-2-pyrimidinone-2'-deoxyribose | Orphan Designation | - |
| glioma susceptibility 2 | 5-iodo-2-pyrimidinone-2'-deoxyribose | Orphan Designation | - |
| malignant glioma | 5-iodo-2-pyrimidinone-2'-deoxyribose | Orphan Designation | - |