2
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| acute lymphoblastic leukemia | Phyrago | Orphan Designation | - |
| chronic myelogenous leukemia, BCR-ABL1 positive | Phyrago | Orphan Designation | - |
| pediatric acute-onset neuropsychiatric syndrome | Phyrago | Orphan Designation | - |
| pediatric hepatocellular carcinoma | Phyrago | Orphan Designation | - |
| pediatric ovarian dysgerminoma | Phyrago | Orphan Designation | - |
| pediatric ovarian germ cell tumor | Phyrago | Orphan Designation | - |
| pediatric-onset Graves disease | Phyrago | Orphan Designation | - |