4
Orphan Designations
0
FDA Approvals
10
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| 22q11.2 deletion syndrome | Cannabidiol | Orphan Designation | - |
| chromosome 22q11.2 deletion syndrome, distal | Cannabidiol | Orphan Designation | - |
| fragile X syndrome | cannabidiol | Orphan Designation | - |
| idiopathic hypersomnia | pitolisantWAKIX® | Orphan Designation | - |
| narcolepsy | WAKIX® | Orphan Designation | - |
| narcolepsy 7 | WAKIX® | Orphan Designation | - |
| narcolepsy without cataplexy | WAKIX® | Orphan Designation | - |
| non-24-hour sleep-wake syndrome | WAKIX® | Orphan Designation | - |
| obesity-hypoventilation syndrome | WAKIX® | Orphan Designation | - |
| velocardiofacial syndrome | Cannabidiol | Orphan Designation | - |