1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| ALK+ histiocytosis | Alecensa | Orphan Designation | - |
| ALK-positive anaplastic large cell lymphoma | Alecensa | Orphan Designation | - |
| ALK-positive large B-cell lymphoma | Alecensa | Orphan Designation | - |
| Bicervical bicornuate uterus with patent cervix and vagina | Alecensa | Orphan Designation | - |
| Yunis-Varon syndrome | Alecensa | Orphan Designation | - |
| carbon monoxide-induced delayed encephalopathy | Alecensa | Orphan Designation | - |