1
Orphan Designations
0
FDA Approvals
8
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Bicervical bicornuate uterus with patent cervix and vagina | RAVICTI | Orphan Designation | - |
| Potocki-Lupski syndrome | RAVICTI | Orphan Designation | - |
| Roberts-SC phocomelia syndrome | RAVICTI | Orphan Designation | - |
| carbon monoxide-induced delayed encephalopathy | RAVICTI | Orphan Designation | - |
| chromosome 14q11-q22 deletion syndrome | RAVICTI | Orphan Designation | - |
| multiple congenital anomalies-hypotonia-seizures syndrome 2 | RAVICTI | Orphan Designation | - |
| multisystemic smooth muscle dysfunction syndrome | RAVICTI | Orphan Designation | - |
| natal teeth-intestinal pseudoobstruction-patent ductus syndrome | RAVICTI | Orphan Designation | - |