1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| alveolar capillary dysplasia with misalignment of pulmonary veins | tucidinostat | Orphan Designation | - |
| neurooculorenal syndrome | tucidinostat | Orphan Designation | - |
| rhizomelic limb shortening with dysmorphic features | tucidinostat | Orphan Designation | - |