2
Orphan Designations
0
FDA Approvals
11
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Bloom syndrome | Erbitux | Orphan Designation | - |
| Diamond-Blackfan anemia 10 | Erbitux | Orphan Designation | - |
| MEGF8-related Carpenter syndrome | Erbitux | Orphan Designation | - |
| Noonan syndrome 10 | Erbitux | Orphan Designation | - |
| Noonan syndrome 8 | Erbitux | Orphan Designation | - |
| local anesthetic poisoning | Erbitux | Orphan Designation | - |
| malignant pancreatic neoplasm | cetuximab | Orphan Designation | - |
| squamous cell carcinoma of colon | Erbitux | Orphan Designation | - |
| squamous cell carcinoma of penis | Erbitux | Orphan Designation | - |
| squamous cell carcinoma of rectum | Erbitux | Orphan Designation | - |
| squamous cell carcinoma of the small intestine | Erbitux | Orphan Designation | - |