5
Orphan Designations
0
FDA Approvals
13
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Down syndrome | Immune globulin intravenous (human) | Orphan Designation | - |
| acquired purpura fulminans | Protein C concentrate | Orphan Designation | - |
| blue toe syndrome | Protein C concentrate | Orphan Designation | - |
| carbon monoxide-induced delayed encephalopathy | Immune globulin intravenous (human) | Orphan Designation | - |
| cholesterol embolism | Protein C concentrate | Orphan Designation | - |
| dermatomyositis | Immune globulin intravenous (human) | Orphan Designation | - |
| juvenile idiopathic arthritis | Immune globulin intravenous (human) | Orphan Designation | - |
| juvenile polymyositis | Immune globulin intravenous (human) | Orphan Designation | - |
| multiple congenital anomalies-hypotonia-seizures syndrome 2 | Immune globulin intravenous (human) | Orphan Designation | - |
| polymyositis | Immune globulin intravenous (human) | Orphan Designation | - |
| purpura | Protein C concentrate | Orphan Designation | - |
| purpura fulminans | Protein C concentrate | Orphan Designation | - |
| vitamin K-antagonist embryofetopathy | Protein C concentrate | Orphan Designation | - |