1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| hepatic fibrosis-renal cysts-intellectual disability syndrome | Disaccharide tripeptide glycerol dipalmitoyl | Orphan Designation | - |
| hepatic vascular disorder | Disaccharide tripeptide glycerol dipalmitoyl | Orphan Designation | - |
| pulmonary alveolar proteinosis | Disaccharide tripeptide glycerol dipalmitoyl | Orphan Designation | - |
| pulmonary arterial hypertension | Disaccharide tripeptide glycerol dipalmitoyl | Orphan Designation | - |
| pulmonary fibrosis | Disaccharide tripeptide glycerol dipalmitoyl | Orphan Designation | - |
| pulmonary hypertension | Disaccharide tripeptide glycerol dipalmitoyl | Orphan Designation | - |