2
Orphan Designations
0
FDA Approvals
4
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| Naxos disease | Atibuclimab | Orphan Designation | - |
| amyotrophic lateral sclerosis | chimeric IgG4 monoclonal antibody targeting CD14 | Orphan Designation | - |
| arrhythmogenic right ventricular cardiomyopathy | Atibuclimab | Orphan Designation | - |
| arrhythmogenic right ventricular dysplasia 8 | Atibuclimab | Orphan Designation | - |