2
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| carbon monoxide-induced delayed encephalopathy | oral potent and selective antagonist | Orphan Designation | - |
| malignant carotid body paraganglioma | retaspimycin | Orphan Designation | - |
| multisystemic smooth muscle dysfunction syndrome | oral potent and selective antagonist | Orphan Designation | - |
| natal teeth-intestinal pseudoobstruction-patent ductus syndrome | oral potent and selective antagonist | Orphan Designation | - |
| post-treatment Lyme disease syndrome | retaspimycin | Orphan Designation | - |
| treatment-refractory schizophrenia | retaspimycin | Orphan Designation | - |