1
Orphan Designations
0
FDA Approvals
6
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| DYRK1A-related intellectual disability syndrome | carbon monoxide | Orphan Designation | - |
| anosmia for isobutyric acid | carbon monoxide | Orphan Designation | - |
| double nail for fifth toe | carbon monoxide | Orphan Designation | - |
| neuroacanthocytosis | carbon monoxide | Orphan Designation | - |
| neurodevelopmental disorder with thin corpus callosum, hypotonia, and absent language | carbon monoxide | Orphan Designation | - |
| osteoporosis-pseudoglioma syndrome | carbon monoxide | Orphan Designation | - |