1
Orphan Designations
0
FDA Approvals
3
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| mucopolysaccharidosis type 6 | odiparcil | Orphan Designation | - |
| mucopolysaccharidosis type 6, rapidly progressing | odiparcil | Orphan Designation | - |
| mucopolysaccharidosis type 6, slowly progressing | odiparcil | Orphan Designation | - |