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Iovance Biotherapeutics, Inc — Rare Disease Pipeline | Kisho | Kisho
Iovance Biotherapeutics, Inc
Other
5
Orphan Designations
1
FDA Approvals
18
Rare Diseases
0
News Articles
Pipeline
Designations
News
Diseases
Disease
Drug(s)
Designation
Approved
MPDU1-congenital disorder of glycosylation
Amtagvi
Orphan Designation
-
Wolf-Hirschhorn syndrome
Aldesleukin
Orphan Designation
-
adult neuronal ceroid lipofuscinosis
Amtagvi
Orphan Designation
-
adult pleomorphic rhabdomyosarcoma
Amtagvi
Orphan Designation
-
adult-onset non-insulinoma persistent hyperinsulinemic hypoglycemia
Amtagvi
Orphan Designation
-
amyotrophic lateral sclerosis
Aldesleukin
Orphan Designation
-
cancer-associated retinopathy
Amtagvi
Orphan Designation
-
cerebellar dysfunction with variable cognitive and behavioral abnormalities
autologous tumor infiltrating lymphocytes (TIL)
Orphan Designation
-
cutaneous melanoma
Amtagvi
Orphan Designation
-
double nail for fifth toe
Aldesleukin
Orphan Designation
-
familial papillary thyroid carcinoma with renal papillary neoplasia
autologous tumor infiltrating lymphocytes (TIL)
Orphan Designation
-
inborn error of immunity
Aldesleukin
Orphan Designation
-
malignant carotid body paraganglioma
Aldesleukin
Orphan Designation
-
malignant cornea melanoma
Amtagvi
Orphan Designation
-
malignant melanoma of the mucosa
Amtagvi
Orphan Designation
-
primary adult heart tumor
Amtagvi
Orphan Designation
-
rectum malignant melanoma
Amtagvi
Orphan Designation
-
uterine cervix carcinoma in situ
autologous tumor infiltrating lymphocytes (TIL)
Orphan Designation
-
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