3
Orphan Designations
0
FDA Approvals
7
Rare Diseases
0
News Articles
| Disease | Drug(s) | Designation | Approved |
|---|---|---|---|
| primary biliary cholangitis | Iqirvo | Orphan Designation | - |
| primary biliary cholangitis 1 | Iqirvo | Orphan Designation | - |
| primary biliary cholangitis 2 | Iqirvo | Orphan Designation | - |
| primary biliary cholangitis 4 | Iqirvo | Orphan Designation | - |
| primary biliary cholangitis/primary sclerosing cholangitis and autoimmune hepatitis overlap syndrome | Iqirvo | Orphan Designation | - |
| primary sclerosing cholangitis | elafibranor | Orphan Designation | - |
| small cell lung carcinoma | irinotecan liposome injection | Orphan Designation | - |